It’s a devastating diagnosis that changes a child’s life — and their family’s — forever. Duchenne Muscular Dystrophy, or DMD, is a rare and fatal genetic disease that primarily affects boys, slowly ...

Parents of a boy with Duchenne Muscular Dystrophy are toasting another boost to their campaign to find a cure, with a new ...

While right-wing populism surges in some of the world’s leading democracies, Chile’s leftist government is rushing in the ...

At age 2, Cal Carr was already reaching developmental milestones later than expected — and then she started regressing.

The symposium took place on 18 th March 2025, as part of the Muscular Dystrophy Association (MDA) Clinical & Scientific ...

Rodriguez confirmed Adama had Duchenne muscular dystrophy. Gibriel's genetic test results are pending. Children often lose ...

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the importance ...

The U.S. Food and Drug Administration (FDA) has cleared Sarepta Therapeutics to start dosing and screening in a first clinical trial testing the gene therapy SRP-9005 in people with limb-girdle ...

This study was funded by the Azrieli Foundation, the National Institutes of Health (NIH), Myotonic Dystrophy Foundation, Muscular Dystrophy Association, the UNVL startup fund, the University of ...

Had I not been a physical therapist, my concerns might have been dismissed, further delaying his devastating Duchenne muscular dystrophy diagnosis ... but a simple blood test through the routine ...

Michael Rankin, 12, has Duchenne Muscular Dystrophy, a condition which causes progressive muscle weakness. He has been using a wheelchair for five years now. He can still walk but only for very ...

According to Ashish Karundia, founder of the CA firm Ashish Karundia & Associates, "Invoking the principal purpose test (PPT), once notified, would be comparatively easier than applying GAAR, as PPT ...