WVE-N531 demonstrated statistically significant improvements in muscle biopsy measures and functional measures in patients ...

DMD is an inherited (passed down ... a sign of muscle cell damage. A muscle biopsy (tissue sample) is usually taken from the ...

As it gears up to submit an approval application next year, Wave Life Sciences has presented fresh phase 2 data showing its ...

Participants in the FORWARD-53 trial had clinically significant improvements in time-to-rise, among other metrics.

meaning disease-modifying DMD therapies need to target skeletal, respiratory, and cardiac muscle, the authors explained. Although a mouse model of DMD showed an improvement in cardiac measures and ...

Muscle biopsy is a minor surgical procedure that involves making an incision in the skin to obtain a few small pieces of the underlying muscle for detailed histologic, histochemical, or biochemical ...

DMD, a genetic disorder affecting 1 in 5000 male births, is caused by mutations in the DMD gene. While it primarily leads to muscle wasting, a new paper published in Molecular Medicine highlights ...

Newborns in Minnesota can now be screened for Duchenne muscular dystrophy (DMD ... treatment can make symptoms and muscle breakdown less severe. A new gene therapy shows positive signs of slowing ...

3 Dystrophin is a critical component of the dystrophin-associated protein complex (DAPC) which supports the strength, stability, function and repair of muscle cells. In DMD, muscle fibres are ...

If the doctor suspects DMD, they’ll likely refer you to a neuromuscular specialist for further screening, which may include a blood test, DNA testing, and a muscle biopsy. Blood testing can ...