CONNECT1 has enrolled two cohorts of boys and young men living with DMD amenable to exon 51 skipping and its ... "As of January 23, 2025, all treatment related adverse events in CONNECT1 have ...

CONNECT1 has enrolled two cohorts of boys and young men living with DMD amenable to exon 51 skipping and its ... “As of January 23, 2025, all treatment related adverse events in CONNECT1 have ...

Paul Streck, MD, Head of R&D, commented, “As of January 23, 2025, all treatment related ... for the treatment of patients with DMD amenable to an exon-51 skipping approach.

today provided recent updates on its CONNECT clinical program investigating PGN-EDO51 in Duchenne muscular dystrophy (DMD) for patients amenable to an exon-51 skipping approach.

Multiple companies are digging in to add the next generation of exon skippers, gene therapies and medicines targeting more than skeletal muscle to their DMD pipelines, and for Michael Kelly, chief ...

Some types of muscular dystrophy can be fatal. Certain types, including Duchenne muscular dystrophy, can lead to problems with the heart and muscles used for breathing. Some people with MD may develop ...

23 January, 1983 Birth of Nara Lokesh, son of former Andhra Pradesh Chief Minister Nara Chandrababu Naidu, continuing the family's political legacy.