Mammoth Biosciences researchers have developed NanoCas, an ultracompact CRISPR nuclease, demonstrating its ability to perform ...
By Balambal Suryanarayanan CRISPR-Cas9 is a repurposed gene editing tool that allows scientists to cut, replace, and insert pieces of DNA in precise regions along the strand. Courtesy of NIH Image ...
Technological advances have reduced genome sequencing costs to $600 ... (AOC 1044), a treatment for people living with Duchenne muscular dystrophy amenable to exon 44 (DMD44).
To explore transcriptomic factors driving differential gene expression and modulating DMD skeletal ... Lastly, we integrate our findings with DMD RNA sequencing data from the TA, and identify ...
Solid Biosciences has surged back into the Duchenne muscular dystrophy (DMD) gene therapy race. | Solid Biosciences has ...
Muscular dystrophy is a disease caused by a genetic mutation. The muscles of muscular dystrophy patients weaken.. | Genetics And Genomics ...
A genetic study published on Tuesday offers an important new clue. Researchers found that, between 250,000 and 500,000 years ...
Gene therapies have set a high bar for outcomes in pharma by delivering curative treatments for difficult diseases in a one-and-done punch. But for Duchenne muscular dystrophy, the results of ...
A new discovery offers hope for Huntington’s disease. This discovery provides hope that a DNA repair process may help slow or ...
Researchers at the University of Toronto have invented a new method that uses DNA sequencing to measure metabolites. This enables rapid and precise analysis of biological compounds, such as sugars, ...
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