The FDA has communicated to Stealth BioTherapeutics that it would not meet elamipretide’s PDUFA target date for the treatment of Barth syndrome.

Stealth BioTherapeutics had expected the FDA to respond on Tuesday to its marketing application for elamipretide to treat ...

Mimi Ward, from Middle Barton, completed the 286-mile, four-day journey in October, raising almost £20,000 for Dravet Syndrome UK. Her efforts were inspired by her eight-year-old cousin ...

SPOILER ALERT: This post contains details about the final episode of Celebrity Big Brother UK 2025. After three weeks of living inside the Celebrity Big Brother UK house, the British public has ...

Since 2022, she has also run 2km every day in the month of May as part of her efforts for the charity Dravet Syndrome UK. The One Show, external took Mimi on a helicopter tour over London before ...

Poppy, from near Folkestone in Kent, was referred to Clinical Genetics at Guy’s Hospital in London, where at the age of two she was diagnosed with Rett Syndrome. The incurable disease impacts ...

Metabolic syndrome is defined as having excess belly fat plus two or more of the following risk factors: high blood pressure, high blood sugar, higher than normal triglycerides, which are a type ...

Ticks can carry a range of illnesses with varying effects, but one of the most deadly is alpha-gal syndrome. The condition is new to the UK with the first reported cases only being noted in 2019 ...

There is a simple discount patient access scheme for leniolisib. NHS organisations can get details on the Commercial Access and Pricing (CAP) Portal. Non-NHS organisations can contact ...

Ticks can carry a range of illnesses with varying effects, but one of the most deadly is alpha-gal syndrome. The condition is new to the UK with the first reported cases only being noted in 2019 ...

After a successful launch last year in the US, Wahoo’s award-winning treadmill, the KICKR RUN Smart Treadmill, has finally arrived on UK soil. The tech-savvy running machine has become highly ...

"It turns out I was allergic to a lot of different foods." Finally in January 2005, Chloe was diagnosed with oral allergy syndrome (OAS) at Solihull Hospital. This meant she was allergic to any pollen ...