Despite significant advancements in spinal muscular atrophy (SMA) management, unmet needs persist, especially for patients ...

Parents of children with spinal muscular atrophy (SMA), a rare disease, welcomed the announcement by the Indian pharma ...

FDA-approved treatments for spinal muscular atrophy differ in their mechanisms of action, safety profiles, and administration ...

Affordable generic version of SMA drug Risdiplam soon available in India, offering hope to patients and activists.

Reason for decision Anticipate the topic will be of importance to patients, carers, professionals, commissioners and the health of the public to ensure clinical benefit is realised, inequalities in ...

Manchester United captain Bruno Fernandes has issued a message after he was joined by a disabled mascot at Old Trafford ahead ...

Funding medical research is about more than just numbers. It's real people,” says Ryan Manriquez, president of the UC ...

It's that time of year when you can become a Hero for Hope and donate to ABC15's annual Telethon for Phoenix Children's ...

Imagine the joy of holding your newborn for the first time, only to hear doctors say your baby would live to the age of two.

The pharmaceutical company says it will continue to operate its production facility near Research Triangle Park.