Caregivers of people with Duchenne muscular dystrophy may play an important role in the prevention and management of fat ...

As Helena Brisby dozed off on Monday afternoon, she was awakened by the smell of smoke and rushed to her son's room, where the sight of flames from the deck on fire was horrifying.

Ann Blake, from Godshill, suffers from muscular dystrophy and released a book in 2024 titled 'A Legacy of Love' to share ...

Leah Messer opens up about feeling conflicted in letting Ali assert her independence when the teen, who lives with muscular ...

Barbara Goodfriend, 83, opted for medical aid in dying after being diagnosed with ALS. The New Jersey widow ended her life in ...

Scholar Rock submitted its BLA of apitegromab for the treatment of patients with Spinal Muscular Atrophy with a request for ...

The Elevate-44-201 study is a global, two-part, randomized, double-blind placebo-controlled phase 1/2 study evaluating the ...

Executive director and ‘chief energy officer’ brings positivity, servant leader mentality to David’s Refuge, a nonprofit ...

The Health and Human Services Office of Inspector General has found that, in a few cases, FDA officials veered from the accelerated approval pathway.

"This type of gene editing should also allow for the treatment of diseases whose origin is not genetic or whose origin cannot ...

usz.ch Background: Duchenne muscular dystrophy (DMD) leads to progressive impairment of ... progressive symmetrical muscle weakness and other signs and symptoms starting before the age of 5 years; ...