Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec.

To help neurologists, clinicians and families understand the current evidence for a new gene therapy for Duchenne muscular ...

Groundbreaking gene therapy offers hope for a boy with fatal muscular dystrophy, potentially slowing disease progression and ...

By combining multiple cutting-edge DNA sequencing methods, the researchers uncovered parts of the genome that mutate far faster than previously thought – findings that could reshape our understanding ...

provides statistically and clinically meaningful treatment benefits in individuals with Duchenne muscular dystrophy (DMD) If approved by the European Commission, Duvyzat will be available for ...

Prostate cancer has distinct genetic properties in different groups of men that can be targeted to improve patient outcomes, UVA Cancer Center researchers have discovered. Based on new findings in ...

We still have maybe 15% or so of people who come to our clinic that we're not able to establish the cause of their muscular dystrophy ... and new discovery in the genetic space for those individuals.

and a rare genetic condition called myotonic dystrophy type 1 (DM1). The study, published today in Nature Neuroscience, suggests that while ASD has previously been characterized by a loss of gene ...

until now. In Dawn of the Hunt, players will cleanse the corruption spreading across Atlas maps via the Corrupted Nexus—featuring three challenging bosses—and unlock additional challenges and ...

There are seven additional endgame maps to clear, farm for loot, and challenge you until you tear some hair out in frustration. You'll spend loads of time running through The Fractured Lake ...

It’s been nearly two years since Elevidys (delandistrogene moxeparvovec-rokl), a gene therapy for Duchenne muscular dystrophy (DMD) developed by Sarepta Therapeutics, was approved by the U.S. Food and ...