Tikun Therapeutics Inc. has obtained U.S. orphan drug and rare pediatric disease designations for its programs in familial dysautonomia, namely its rAAV2-U1a-hELP1 gene replacement therapy for the ...
This discovery comes from a group of researchers in the United States studying a rare genetic disease called familial dysautonomia. This condition, which affects the peripheral nervous system ...
Cette infatigable militante a notamment été présidente du Planning familial américain de 2006 à 2018. L’ancienne présidente du Planning familial américain Cecile Richards est décédée ...
Based on our initial experience with this population, we evaluated the presentation rates of 13 diagnoses: CMI, TCS, POTS, MCAD, dysautonomia, myalgic encephalomyelitis/chronic fatigue syndrome ...
Parmi les alternatives, le prêt familial ou amical est une solution légale pour solliciter ses proches, à condition d'en respecter les règles et de prendre certaines précautions pour éviter les ...
The condition is known as familial dysautonomia, which becomes evident during infancy. The hypothesis of this relatively large cadre of regenerative medicine researchers is that genipin from the ...
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