Duchenne muscular dystrophy (DMD) is a rare neurological ... a sign of muscle cell damage. A muscle biopsy (tissue sample) is usually taken from the thigh muscle. Biopsy imaging examines muscle ...

A trial found magnetic resonance imaging correlated with physical function tests in patients with Duchenne muscular dystrophy ...

DMD treatment KER-065 showed a good safety profile in a Phase 1 clinical trial with no serious side effects seen in healthy ...

WVE-N531 showed significant improvements in functional measures and muscle health in DMD patients during the ... and the data demonstrated a 61-day tissue half-life that supports a once-monthly ...

As it gears up to submit an approval application next year, Wave Life Sciences has presented fresh phase 2 data showing its Duchenne muscular dystrophy (DMD) therapy is up to the task. The latest ...

Becker muscular dystrophy (BMD) is a type of muscular dystrophy, a genetic condition that weakens and damages muscles. It can worsen with age. However, its symptoms are less severe than those of ...

Duchenne Muscular Dystrophy: diagnosis, clinical development and global researchMuscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, ...

None of the eteplirsen-treated patients reached a left ventricular ejection fraction below 50% compared with 22.1% of patients in the control group.

Company will temporarily pause CONNECT2 and focus efforts on ongoing CONNECT1-EDO51 study of PGN-EDO51 in DMD, with 10 mg/kg ... exon skipping, and muscle tissue concentration.

In DMD, muscle fibres are highly susceptible to injury ... impairment of muscle regeneration and muscle replacement by fibrotic and fat tissue. 4, 5-7 The disease primarily affects boys, with ...

Early screening for Duchenne muscular dystrophy can help you get early treatments and referrals for your child to help prevent further loss of muscle tissue. Duchenne muscular dystrophy (DMD ...