Recent studies have shed light on the critical role of cardiolipin in mitochondrial function and how its deficiency can lead to severe health issues in Barth syndrome. For instance, one study ...

The FDA has extended the review period for the New Drug Application for elamipretide for the treatment of Barth syndrome.

A US Food and Drug Administration (FDA) advisory committee (AdCom) has voted in support of Stealth Biotherapeutics’ ...