X-linked adrenoleukodystrophy (X-ALD) is a debilitating disease caused by mutations in the ABCD1 gene. Approximately 30% of affected boys develop the progressive ...

Adrenoleukodystrophy (ALD) is rare X-linked genetic disease that affects the adrenal glands (found on top of the kidneys) as well as the myelin in the brain and spinal cord. The incidence of ALD ...

X-linked adrenoleukodystrophy (X-ALD) is a genetic condition passed through families on the X chromosome. The name “Adrenoleukodystrophy” can be broken into three parts: “Adreno” refers to ...

Dublin, Dec. 07, 2020 (GLOBE NEWSWIRE) -- The "Adrenoleukodystrophy (ALD) - Epidemiology Forecast to 2030" report has been added to ResearchAndMarkets.com's offering. This 'Adrenoleukodystrophy ...

An FDA advisory panel recommended the agency approve elivaldogene autotemcel (eli-cel), an investigational gene therapy, for select children with cerebral adrenoleukodystrophy (ALD), arguing that ...

Viking Therapeutics Inc. on Wednesday reported positive data from an early-stage trial of a treatment for the rare, and often fatal, metabolic disorder X-linked adrenoleukodystrophy, or X-ALD.

Cerebral adrenoleukodystrophy is a severe form of ... (Funded by Bluebird Bio; ALD-102 and LTF-304 ClinicalTrials.gov numbers NCT01896102 and NCT02698579, respectively.) Autologous hematopoietic ...

After a series of tests and consultations, they received the life-changing diagnosis: their son had X-linked Adrenoleukodystrophy, or ALD, a rare and serious genetic disorder. "You're left ...

This is also the case for X-linked adrenoleukodystrophy (or X-ALD), an inherited condition that affects 6 to 8 out of every 100,000 births. It is characterized by an excessive accumulation of very ...

HSCT may be a suitable treatment for X-linked ALD adults with early signs of cerebral involvement. Very long-chain fatty acid levels and adrenoleukodystrophy protein (ALDP)-deficiency are strongly ...